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Title |
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| Vol 6, No 2 (2025) |
Consensus on implementation features of the Russian-manufactured generic Nusinersen (TN Lantesens) for SMA 5q treatment in Russia |
Abstract
PDF (Rus)
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Dina V. Ayzatulina, Svetlana B. Artemyeva, Dmitry V. Vlodavets, Ekaterina I. Karpovich, Darya G. Korotkova, Lyudmila M. Kuzenkova, Oleg L. Lapochkin, Viktoriya S. Lobanova, Svetlana V. Mikhailova, Kristina S. Nevmerzhitskaya, Sofia G. Popovich, Natalia S. Smirnova, Irina B. Sosnina, Eugeniya V. Uvakina |
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| Vol 2, No 1 (2021) |
Consensus on gene replacement therapy for spinal muscular atrophy |
Abstract
PDF (Rus)
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S. B. Artemyeva, E. D. Belousova, D. V. Vlodavets, V. I. Guzeva, L. M. Kuzenkova, S. I. Kutsev, A. V. Marakhonov, N. L. Pechatnikova, A. V. Polyakov |
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| Vol 3, No 4 (2022) |
Expert council resolution on the use of pathogenetic therapy with Ataluren in patients with non-ambulatory Duchenne muscular dystrophy |
Abstract
PDF (Rus)
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Svetlana B. Artemyeva, Dmitry V. Vlodavets, Valentina I. Guzeva, Altynshash K. Dzhaksybayeva, Irina V. Zhauniaronak, Ludmila M. Kuzenkova, Marzhan M. Lepessova, Bakhyt D. Myrzalieva, Natalia L. Pechatnikova, Tatyana V. Podkletnova, Vasily M. Suslov, Irina V. Pelipenko, Luca Bello, Niculina Butoianu |
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| Vol 4, No 2 (2023) |
Consensus on Gene Replacement Therapy for the Treatment for Spinal Muscular Atrophy |
Abstract
PDF (Rus)
PDF (Eng)
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