INFORMATIONAL MATERIALS
Issue | Title | |
Vol 2, No 1 (2021) | Consensus on gene replacement therapy for spinal muscular atrophy | Abstract PDF (Rus) |
S. B. Artemyeva, E. D. Belousova, D. V. Vlodavets, V. I. Guzeva, L. M. Kuzenkova, S. I. Kutsev, A. V. Marakhonov, N. L. Pechatnikova, A. V. Polyakov | ||
Vol 3, No 4 (2022) | Expert council resolution on the use of pathogenetic therapy with Ataluren in patients with non-ambulatory Duchenne muscular dystrophy | Abstract PDF (Rus) |
Svetlana B. Artemyeva, Dmitry V. Vlodavets, Valentina I. Guzeva, Altynshash K. Dzhaksybayeva, Irina V. Zhauniaronak, Ludmila M. Kuzenkova, Marzhan M. Lepessova, Bakhyt D. Myrzalieva, Natalia L. Pechatnikova, Tatyana V. Podkletnova, Vasily M. Suslov, Irina V. Pelipenko, Luca Bello, Niculina Butoianu | ||
Vol 4, No 2 (2023) | Consensus on Gene Replacement Therapy for the Treatment for Spinal Muscular Atrophy | Abstract PDF (Rus) PDF (Eng) |
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