For citations:
Fisenko D.A., Kurenkov A.L., Kuzenkova L.M., Chernikov V.V., Uvakina E.V., Popovich S.G., Bursagova B.I., Abdullaeva L.M., Kurova J.A., Adalimova N.S., Nikolenko D.S., Globa O.V., Andreenko N.V. The efficacy of gene therapy with onasemnogene abeparvovec in spinal muscular atrophy in young patients. L.O. Badalyan Neurological Journal. 2025;6(1):13-25. (In Russ.) https://doi.org/10.46563/2686-8997-2025-6-1-13-25. EDN: yyenrs